Verified source report
STAT+: Five years after disaster, a rare disease community gets new chance at treatment
Some boys had astonishing recoveries. But other boys died. Now Astellas is returning to revised gene therapy for XLMTM.
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Some boys had astonishing recoveries. But other boys died. Now Astellas is returning to revised gene therapy for XLMTM.
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What happened
According to STAT’s source item, STAT+: Five years after disaster, a rare disease community gets new chance at treatment, Some boys had astonishing recoveries. But other boys died. Now Astellas is returning to revised gene therapy for XLMTM.
Context
The development sits in VINI’s Science file for readers following research, health, climate, space, medicine, and scientific institutions. The original report is linked so readers can check the source account, follow later updates, and compare new coverage against the first published record. The source item is dated 2026-05-11T08:30:00+00:00.
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Source
Primary source: STAT+: Five years after disaster, a rare disease community gets new chance at treatment via STAT. VINI cites and links the source; it does not reproduce the publisher’s full article text without rights clearance.
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- STAT+: Five years after disaster, a rare disease community gets new chance at treatmentSTAT - 2026-05-11T08:30:00+00:00
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